New study suggests base editing may be an effective one-time, durable treatment for inherited retinal degeneration

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New study suggests base editing may be an effective one-time, durable treatment for inherited retinal degeneration

A new University of California, Irvine-led study indicates base editing may provide long-lasting retinal protection and prevent vision deterioration in patients with inherited retinal degeneration, specifically in Leber congenital amaurosis (LCA) patients. 

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